Zynbera is enrolling FXS patients in the US, Australia and New Zealand for CONNECT-FX study that will evaluate its CBD gel ZYN002. The Devon, Philadelphia-based pharma company expects to report top-line data in the second half of 2019.
Fragile X syndrome (FXS) is a genetic disorder that affects both males and females. As of now, there is no cure for FXS, which causes intellectual disability, behavioral and learning challenges, and developmental delays in children.
About 71,000 US patients are believed to have FXS, based on FXS prevalence estimates of approximately 1 in 3,600 to 4,000 in males and of approximately 1 in 4,000 to 6,000 in females.
The company also expects to announce top-line data results from the other three childhood neuropsychiatric studies in the next two years (one in the third quarter of 2019 and two in the first half of 2020).
Zynerba stock, which ended Monday’s trading session down 1.56% at $5.04, had jumped 70% since the beginning of 2019.
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